UPSC MainsMANAGEMENT-PAPER-II202110 Marks
Q18.

Statistical Significance: Drug vs. Sugar Pills

A certain drug is claimed to be effective in curing cold. In an experiment on 500 persons suffering from cold, half of them were given the drug and the other half were given the sugar pills. Patients' reactions to the treatment are recorded in the following table: Treatment Helped Harmed No Effect Drug 150 30 70 Sugar pills 130 40 80 Total 280 70 150 On the basis of the above data, can it be concluded that there is a significant difference in the effect of drug and sugar pills ?

How to Approach

This question requires a statistical hypothesis testing approach. We need to determine if the observed difference in the effectiveness of the drug versus the sugar pill is statistically significant, or if it could have occurred by chance. The Chi-Square test is the most appropriate method here. The answer should involve formulating null and alternative hypotheses, calculating the Chi-Square statistic, determining the degrees of freedom, finding the p-value, and then drawing a conclusion based on a pre-defined significance level (usually 0.05). The explanation should be clear and concise, focusing on the interpretation of the results.

Model Answer

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Introduction

In medical research, establishing the efficacy of a new drug requires rigorous testing and statistical analysis. The placebo effect, where a patient experiences a benefit from a treatment with no active medicinal properties, is a well-documented phenomenon. To determine if a drug’s effect is genuine and not simply due to the placebo effect, researchers employ statistical methods to compare the outcomes of a treatment group with a control group receiving a placebo. This question presents data from an experiment designed to assess the effectiveness of a drug against the common cold, and asks us to determine if the observed difference in outcomes between the drug and sugar pill groups is statistically significant.

Hypothesis Formulation

Before conducting the statistical test, we need to formulate the null and alternative hypotheses:

  • Null Hypothesis (H0): There is no significant difference in the effect of the drug and sugar pills. In other words, the drug is no more effective than the placebo.
  • Alternative Hypothesis (H1): There is a significant difference in the effect of the drug and sugar pills. The drug is more effective than the placebo.

Contingency Table and Expected Frequencies

The given data can be represented in a contingency table:

Helped Harmed No Effect Total
Drug 150 30 70 250
Sugar Pills 130 40 80 250
Total 280 70 150 500

To perform the Chi-Square test, we need to calculate the expected frequencies for each cell under the assumption that the null hypothesis is true. The expected frequency for each cell is calculated as:

Expected Frequency = (Row Total * Column Total) / Grand Total

Here's a table showing the calculated expected frequencies:

Helped Harmed No Effect
Drug 140 35 75
Sugar Pills 140 35 75

Chi-Square Statistic Calculation

The Chi-Square statistic (χ2) is calculated using the following formula:

χ2 = Σ [(Observed Frequency - Expected Frequency)2 / Expected Frequency]

Calculating the Chi-Square statistic for each cell and summing them up:

  • For Drug - Helped: (150 - 140)2 / 140 = 100 / 140 = 0.714
  • For Drug - Harmed: (30 - 35)2 / 35 = 25 / 35 = 0.714
  • For Drug - No Effect: (70 - 75)2 / 75 = 25 / 75 = 0.333
  • For Sugar Pills - Helped: (130 - 140)2 / 140 = 100 / 140 = 0.714
  • For Sugar Pills - Harmed: (40 - 35)2 / 35 = 25 / 35 = 0.714
  • For Sugar Pills - No Effect: (80 - 75)2 / 75 = 25 / 75 = 0.333

χ2 = 0.714 + 0.714 + 0.333 + 0.714 + 0.714 + 0.333 = 3.522

Degrees of Freedom and P-value

The degrees of freedom (df) for a contingency table are calculated as:

df = (Number of Rows - 1) * (Number of Columns - 1)

In this case, df = (2 - 1) * (3 - 1) = 1 * 2 = 2

Using a Chi-Square distribution table or a statistical calculator, with a Chi-Square statistic of 3.522 and 2 degrees of freedom, the p-value is approximately 0.171.

Conclusion

We typically use a significance level (α) of 0.05. Since the p-value (0.171) is greater than the significance level (0.05), we fail to reject the null hypothesis. This means that there is not enough evidence to conclude that there is a statistically significant difference in the effect of the drug and sugar pills. The observed difference could be due to random chance.

Conclusion

Based on the statistical analysis of the provided data, we cannot conclude that the drug is significantly more effective than the sugar pills in curing the common cold. The Chi-Square test yielded a p-value greater than the conventional significance level of 0.05, indicating that the observed differences in treatment outcomes could be attributed to random variation. Further research with a larger sample size or a more potent drug formulation might be necessary to establish a statistically significant effect.

Answer Length

This is a comprehensive model answer for learning purposes and may exceed the word limit. In the exam, always adhere to the prescribed word count.

Additional Resources

Key Definitions

Placebo Effect
A beneficial effect produced by a placebo, which cannot be attributed to the placebo itself, and must therefore be due to the patient’s belief in treatment.
Chi-Square Test
A statistical test used to determine if there is a significant association between two categorical variables. It compares the observed frequencies with the expected frequencies under the assumption of independence.

Key Statistics

According to the National Institutes of Health (NIH), approximately 30-77% of patients experience a positive response to placebos in clinical trials. (Source: NIH, 2023 - knowledge cutoff)

Source: National Institutes of Health (NIH)

The global pharmaceutical market was valued at approximately $1.48 trillion in 2022 and is projected to reach $2.25 trillion by 2032. (Source: Grand View Research, 2023 - knowledge cutoff)

Source: Grand View Research

Examples

The Radium Water Craze

In the early 20th century, radium-infused water was marketed as a health tonic, despite having no proven medical benefits. People reported feeling better after drinking it, largely due to the placebo effect and the belief in its curative powers.

Frequently Asked Questions

What is a significance level (alpha)?

The significance level (alpha) is the probability of rejecting the null hypothesis when it is actually true. A common value for alpha is 0.05, meaning there is a 5% chance of making a Type I error (false positive).

Topics Covered

StatisticsMedicineHypothesis TestingChi-Square TestClinical Trials